Regeneron Pharmaceuticals has demonstrated that its gene therapy, DB-OTO, can restore hearing in children born with profound deafness due to OTOF gene mutations. The therapy uses a dual-vector viral system…
Insilico Medicine has advanced the first generative AI-discovered and AI-designed drug candidate into Phase II clinical trials. The drug, INS018_055, targets idiopathic pulmonary fibrosis, a chronic condition that causes progressive…
Vertex Pharmaceuticals has successfully completed Phase 3 trials for suzetrigine, a novel non-opioid pain medication. By targeting specific sodium channels in the peripheral nervous system, the drug blocks pain signals…
